Histiocytic and dendritic cell tumors

2025-07-30   Paola Dal Cin, PhD , Judith Ann Ferry, MD 

1.Brigham and Women's Hospital , Harvard Medical School, Boston , MA (USA)
2.Massachusetts General Hospital/ Harvard Medical School

Keywords
Histiocytic-dendritic cell neoplasm,xanthogranuloma, Erdheim−Chester disease,Rosai−Dorfman disease, Langerhans cell histiocytosis, follicular dendritic cell sarcoma

Classification

Definition

Histiocytic-dendritic cell neoplasms are rare. Those encountered in head and neck region include juvenile xanthogranuloma (JXG}; Erdheim−Chester disease (ECD); Rosai−Dorfman disease RDD); Langerhans cell histiocytosis (LCH) and follicular dendritic cell sarcoma. Most published reports of histiocytic-dendritic cell neoplasms involving the head and neck consist of case reports and small series.

 Molecular genetic studies have linked LCH, ECD and RDD with the identification of somatic mutations of genes in the MAPK-ERK signaling pathway including BRAF, ARAF, MAP2K1, NRAS and KRAS, 1 albeit with highly variable frequencies among the different types of histiocytic diseases. 2
 
LCH, ECD and RDD are distinct pathologic entities. Some questions remain about JXG as an entity, at least in a subset of cases, since BRAF V600E somatic mutations have been detected in cases reported as JXG of the CNS; such cases may be better interpreted as ECD. In addition, clinicopathologic features of cases of ALK+ histiocytosis show some overlap with systemic JXG, 3 performing a stain for ALK in such cases will avoid misdiagnosis.

Histiocytic and dendritic cell tumorsGenetic events
Juvenile xanthogranuloma (JXG)Juvenile xanthogranuloma (JXG) is a non-Langerhans cell histiocytosis, mainly affecting infants and young children. Adults are infrequently affected. Lesions are confined to skin in most cases but extracutaneous involvement, including multiple different head and neck sites, is reported. 4-6 Activating mutations of NRAS, KRAS, ARAF, MAP2K1, and others, and NTRK1 and BRAF gene fusions, have been reported. 7-9 JXG-like histopathology with a rare KIF5B::ALK fusion in a subglottic lesion. 10 JXG-like lesions involving the CNS and harboring BRAF V600E mutation may be better classified as Erdheim-Chester disease.11 JXG-like cases with systemic involvement and ALK translocations are better considered to represent ALK+ histiocytosis. 12,13 Several cases of JXG have been reported in children with germline mutations in NF1 , NF2, SLC12A3, PTPN11. The incidence of juvenile myelomonocytic leukemia (JMML) is increased in patients with neurofibromatosis type 1 but the additional finding of JXG in these patients likely does not further increase the risk of JMML.3,14
Erdheim-Chester disease (ECD)Erdheim-Chester disease (ECD) consists of a proliferation of mature neoplastic histiocytes that can involve many different anatomic sites. BRAF V600E is found in the majority of cases. In the absence of mutated BRAF, other mutually exclusive mutations of MAPK and non-MAPK pathway genes MAP2K1KRAS, NRAS or PIK3CA mutations can be identified. 15,16
Rosai-Dorfman disease (RDD)The hallmark of Rosai-Dorfman disease (RDD) is a proliferation of large, S100+ histiocytes with emperipolesis of leukocytes, mostly lymphocytes. Lymph nodes and many different extranodal sites can be involved. Disease can be localized or widespread. Mutations of MAPK/ERK pathway genes are identified in about 50% of the cases; they include  KRAS, NRAS, MAP2K1ARAF, CSF1R and rarely BRAF V600E mutation. 16-18
Langerhans cell histiocytosis (LCH)Langerhans cell histiocytosis (LCH) is a neoplasm of dendritic cells with the immunophenotype of Langerhans cells.(S100+, CD1a+, CD207+) Patients may have single-system or multisystem disease. Common sites of involvement include skin and bone; lymph nodes and multiple other extranodal sites can be involved.19,20 MAPK pathway mutations are usually detected, with BRAF V600E being the most common , followed by MAP2K1 and more rarely, ARAF ,ERBB3, NRAS, and KRAS mutations. MAP2K1 and BRAF mutations are mutually exclusive. 16,21
Follicular dendritic cell sarcoma (FDCS)Follicular dendritic cell sarcoma (FDCS) is a low-grade malignant neoplasm composed of stroma-derived cells recapitulating the FDC normally residing in germinal centers. It most often affects lymph nodes but extranodal sites can be involved.22 The mutational spectrum is somewhat heterogeneous. MAPK pathway mutations are rare, while NF-κB pathway mutations are common, with NFKBIA inactivation as the most common genetic alteration followed by BIRC3 , NFKBIA, TRAF3, SOCS3 and TNFAIP3. Other alterations affect CDKN2A and TP53. Fusions are uncommon. 23-26

Article Bibliography

Reference NumberPubmed IDLast YearTitleAuthors
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3353784092022Juvenile and adult xanthogranuloma: A 30-year single-center experience and review of the disorder and its relationship to other histiocytoses.Salari B et al
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12328227922023Systemic juvenile xanthogranuloma has a higher frequency of ALK translocations than BRAFV600E mutations.Xu J et al
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Citation

Paola Dal Cin, PhD ; Judith Ann Ferry, MD

Histiocytic and dendritic cell tumors

Atlas Genet Cytogenet Oncol Haematol. 2025-07-30

Online version: http://atlasgeneticsoncology.org/solid-tumor/209330/histiocytic-and-dendritic-cell-tumors